Young Investigators Symposium

14:00 • S5L1 • Delivery and expression of large dystrophins using adeno-associated viral vector and protein trans-splicing mediated by split inteins > H. Hichem TASFAOUT 14:15 • S5L2 • Novel AAV capsid variant for muscle-directed gene therapy > J. Juliette LEMOINE 14:30 • S5L3 • Inactivating the lipid kinase activity of PI3K-C2β is sufficient to rescue X-linked myotubular myopathy in mice > M. Marie GORET 14:45 • S5L4 • PARP3 promotes myogenic differentiation and skeletal muscle function in cooperation with the histone methyltransferase EZH2. > Z. Zuleyha YILDIRIM