Young Investigators Symposium

2:00 PM • S5L1 • Delivery and expression of large dystrophins using adeno-associated viral vector and protein trans-splicing mediated by split inteins > H. Hichem TASFAOUT 2:15 PM • S5L2 • Novel AAV capsid variant for muscle-directed gene therapy > J. Juliette LEMOINE 2:30 PM • S5L3 • Inactivating the lipid kinase activity of PI3K-C2β is sufficient to rescue X-linked myotubular myopathy in mice > M. Marie GORET 2:45 PM • S5L4 • PARP3 promotes myogenic differentiation and skeletal muscle function in cooperation with the histone methyltransferase EZH2. > Z. Zuleyha YILDIRIM