Advances and challenges in gene therapies (part 2)

14:30 • S12L1 • X-linked myotubular myopathy and liver dysfunction > A. Ana BUJ-BELLO (Evry, France) 15:00 • S12L2 • Modelling and editing Duchenne Muscular Dystrophy > W-H. Wolfram-Hubertus ZIMMERMANN (Goettingen, Germany) 15:30 • S12L3 • Application of CRISPR/Cas9 strategy for gene therapy of Myotonic Dystrophy type 1 > G. Germana FALCONE (Monterotondo, Italy)